发明名称 |
FUNCTIONALLY-MODIFIED OLIGONUCLEOTIDES AND SUBUNITS THEREOF |
摘要 |
Functionally-modified oligonucleotide analogues comprising modified intersubunit linkages and/or modified 3′ and/or 5′-end groups are provided. The disclosed compounds are useful for the treatment of diseases where inhibition of protein expression or correction of aberrant mRNA splice products produces beneficial therapeutic effects. |
申请公布号 |
HK1201514(A1) |
申请公布日期 |
2015.09.04 |
申请号 |
HK20150102136 |
申请日期 |
2015.03.03 |
申请人 |
SAREPTA THERAPEUTICS INC. |
发明人 |
GUNNAR J. HANSON;DWIGHT D. WELLER;BAO ZHONG CAI;MING ZHOU |
分类号 |
C04B |
主分类号 |
C04B |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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