发明名称 PYRAZOLOPYRIDAZINES AND METHODS FOR TREATING RETINAL-DEGENERATIVE DISEASES AND HEARING LOSS ASSOCIATED WITH USHER SYNDROME
摘要 Compounds, compositions and methods for the treatment of retinal degenerative diseases, such as retinitis pigmentosa, Leber's congenital Amaurosis, Syndromic retinal degenerations, age-related macular degeneration and Usher Syndrome, and hearing loss associated with Usher Syndrome are described herein.
申请公布号 EP2912038(A1) 申请公布日期 2015.09.02
申请号 EP20130849803 申请日期 2013.10.25
申请人 USHER III INITIATIVE, INC. 发明人 BURLI, ROLAND WERNER;ESMIEU, WILLIAM RAMESHCHANDRA KRISHNA;LOCK, CHRISTOPHER JAMES;MALAGU, KARINE FABIENNE;OWENS, ANDREW PATE;HARTE, WILLIAM EDWARD
分类号 C07D487/04;A61K31/5025;A61P43/00 主分类号 C07D487/04
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