<p>The present invention provides a pharmaceutical composition which causes skipping of the 53rd exon in the human dystrophin gene with a high efficiency. The present invention provides an oligomer which efficiently enables to cause skipping of the 53rd exon in the human dystrophin gene.</p>
申请公布号
AU2015203659(A1)
申请公布日期
2015.07.23
申请号
AU20150203659
申请日期
2015.06.30
申请人
NIPPON SHINYAKU CO., LTD.;NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY