发明名称 Antisense nucleic acid
摘要 <p>The present invention provides a pharmaceutical composition which causes skipping of the 53rd exon in the human dystrophin gene with a high efficiency. The present invention provides an oligomer which efficiently enables to cause skipping of the 53rd exon in the human dystrophin gene.</p>
申请公布号 AU2015203659(A1) 申请公布日期 2015.07.23
申请号 AU20150203659 申请日期 2015.06.30
申请人 NIPPON SHINYAKU CO., LTD.;NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY 发明人 WATANABE, NAOKI;SATOU, YOUHEI;TAKEDA, SHIN-ICHI;KOBAYASHI, HIROSHI;NAGATA, TETSUYA
分类号 C12N15/113;A61K31/7125;A61P21/04;C07H21/04 主分类号 C12N15/113
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