发明名称 ASSAYS FOR DIAGNOSING AND EVALUATING TREATMENT OPTIONS FOR FABRY DISEASE
摘要 <p>Abstract Provided are in vitro and in vivo methods for determining whether a patient with Fabry disease will respond to treatment with a specific pharmacological chaperone. co IMU13 S9I.N -OW# DII nBO 6 ow~" I 1"~U113 d OOC L# i11 AM Ili I i i eW.ION 10 %</p>
申请公布号 AU2013205532(A8) 申请公布日期 2015.07.16
申请号 AU20130205532 申请日期 2013.04.12
申请人 NATIONAL INSTITUTES OF HEALTH;AMICUS THERAPEUTICS, INC. 发明人 KANESKI, CHRISTINE;SHIN, SANG-HOON;MURRAY, GARY;LUDWIG, KARIN;LOCKHART, DAVID;CASTELLI, JEFF
分类号 G01N33/53;G01N33/567;G01N33/573 主分类号 G01N33/53
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