ASSAYS FOR DIAGNOSING AND EVALUATING TREATMENT OPTIONS FOR FABRY DISEASE
摘要
<p>Abstract Provided are in vitro and in vivo methods for determining whether a patient with Fabry disease will respond to treatment with a specific pharmacological chaperone. co IMU13 S9I.N -OW# DII nBO 6 ow~" I 1"~U113 d OOC L# i11 AM Ili I i i eW.ION 10 %</p>
申请公布号
AU2013205532(A8)
申请公布日期
2015.07.16
申请号
AU20130205532
申请日期
2013.04.12
申请人
NATIONAL INSTITUTES OF HEALTH;AMICUS THERAPEUTICS, INC.
发明人
KANESKI, CHRISTINE;SHIN, SANG-HOON;MURRAY, GARY;LUDWIG, KARIN;LOCKHART, DAVID;CASTELLI, JEFF