The invention relates to inhibitors of glucosylceramide synthase (GCS) useful for the treatment metabolic diseases, such as lysosomal storage diseases, either alone or in combination with enzyme replacement therapy.
申请公布号
WO2015089067(A1)
申请公布日期
2015.06.18
申请号
WO2014US69338
申请日期
2014.12.09
申请人
GENZYME CORPORATION
发明人
LEONARD, JOHN P.;DELEUZE, JEAN-FRANÇOIS;ITIER, JEAN-MICHEL;ORSINI, CÉCILE;RET-LECUELLE, GWÉNAËLLE;VIALE, SANDRA
