发明名称 METHODS FOR TREATMENT OF MUSCULAR DYSTROPHIES
摘要 The present invention relates to, inter alia, treatment of muscle dystrophy (e.g., Duchenne Muscular Dystrophy), for example, using a composition, e.g., a composition comprising Compound (I), or a pharmaceutically acceptable salt, prodrug or metabolite thereof.
申请公布号 WO2015061685(A1) 申请公布日期 2015.04.30
申请号 WO2014US62178 申请日期 2014.10.24
申请人 BUSH, ERNEST, D.;NIQUE, FRANCOIS;JAGERSCHMIDT, CATHERINE;NAMOUR, FLORENCE, SYLVIE;BLANQUE, ROLAND;LEFRANCOIS, JEAN-MICHAEL;PEIXOTO, CHRISTOPHE;DEPREZ, PIERRE;TRIBALLEAU, NICOLAS;WIGERINCK, PIET, TOM, BURT, PAUL 发明人 BUSH, ERNEST, D.;NIQUE, FRANCOIS;JAGERSCHMIDT, CATHERINE;NAMOUR, FLORENCE, SYLVIE;BLANQUE, ROLAND;LEFRANCOIS, JEAN-MICHAEL;PEIXOTO, CHRISTOPHE;DEPREZ, PIERRE;TRIBALLEAU, NICOLAS;WIGERINCK, PIET, TOM, BURT, PAUL
分类号 A61K31/395 主分类号 A61K31/395
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