摘要 |
The present invention relates to, inter alia, treatment of muscle dystrophy (e.g., Duchenne Muscular Dystrophy), for example, using a composition, e.g., a composition comprising Compound (I), or a pharmaceutically acceptable salt, prodrug or metabolite thereof. |
申请人 |
BUSH, ERNEST, D.;NIQUE, FRANCOIS;JAGERSCHMIDT, CATHERINE;NAMOUR, FLORENCE, SYLVIE;BLANQUE, ROLAND;LEFRANCOIS, JEAN-MICHAEL;PEIXOTO, CHRISTOPHE;DEPREZ, PIERRE;TRIBALLEAU, NICOLAS;WIGERINCK, PIET, TOM, BURT, PAUL |
发明人 |
BUSH, ERNEST, D.;NIQUE, FRANCOIS;JAGERSCHMIDT, CATHERINE;NAMOUR, FLORENCE, SYLVIE;BLANQUE, ROLAND;LEFRANCOIS, JEAN-MICHAEL;PEIXOTO, CHRISTOPHE;DEPREZ, PIERRE;TRIBALLEAU, NICOLAS;WIGERINCK, PIET, TOM, BURT, PAUL |