| 发明名称 |
PERMANENT GENE CORRECTION BY MEANS OF NUCLEOTIDE-MODIFIED MESSENGER RNA |
| 摘要 |
The present invention relates to a nucleotide-modified messenger RNA for the permanent correction of a genetic alteration on a DNA. The invention further relates to a nucleotide- modified messenger RNA in combination with a repair template. It finally relates to a pharmaceutical composition. |
| 申请公布号 |
WO2015052133(A1) |
申请公布日期 |
2015.04.16 |
| 申请号 |
WO2014EP71343 |
申请日期 |
2014.10.06 |
| 申请人 |
EBERHARD KARLS UNIVERSITAET TUEBINGEN MEDIZINISCHE FAKULTAET |
发明人 |
KORMANN, MICHAEL;MAYS, LAUREN |
| 分类号 |
A61K48/00;C07K14/47;C07K14/785;C12N9/22 |
主分类号 |
A61K48/00 |
| 代理机构 |
|
代理人 |
|
| 主权项 |
|
| 地址 |
|
