| 发明名称 | Methods for treatment of Fabry disease | ||
| 摘要 | Provided are in vitro and in vivo methods for determining whether a patient with Fabry disease will respond to treatment with a specific pharmacological chaperone. | ||
| 申请公布号 | US9000011(B2) | 申请公布日期 | 2015.04.07 |
| 申请号 | US201213445338 | 申请日期 | 2012.04.12 |
| 申请人 | Amicus Therapeutics, Inc. | 发明人 | Lockhart David;Castelli Jeff |
| 分类号 | A61K31/45;G01N33/50;A61K45/06;C07D211/46 | 主分类号 | A61K31/45 |
| 代理机构 | Servilla Whitney LLC | 代理人 | Servilla Whitney LLC |
| 主权项 | 1. A method for treatment of Fabry disease in a patient in need thereof comprising administering to the patient a therapeutically effective dose of 150 mg 1-deoxygalactonojirimycin or a salt thereof every other day. | ||
| 地址 | Cranbury NJ US | ||