ALLELE-SPECIFIC RNA SILENCING FOR THE TREATMENT OF HYPERTROPHIC CARDIOMYOPATHY
摘要
Provided herein are methods and compositions useful for the treatment of hypertrophic cardiomyopathy (HCM), dilated cardiomyopathy (DCM) and/or left ventricular non-compaction (LVNC) and other cardiomyopathies through allele-specific RNA silencing.
申请公布号
CA2925242(A1)
申请公布日期
2015.03.26
申请号
CA20142925242
申请日期
2014.09.23
申请人
PRESIDENT AND FELLOWS OF HARVARD COLLEGE;THE BRIGHAM AND WOMEN'S HOSPITAL, INC.
