发明名称 |
MODULATION OF EXON RECOGNITION IN PRE-MRNA BY INTERFERING WITH THE SECONDARY RNA STRUCTURE |
摘要 |
The invention relates to oligonucleotides for inducing skipping of exon 55 of the dystrophin gene. The invention also relates to methods of inducing exon 55 skipping using the oligonucleotides. |
申请公布号 |
US2015080563(A2) |
申请公布日期 |
2015.03.19 |
申请号 |
US201213550210 |
申请日期 |
2012.07.16 |
申请人 |
van Deutekom Judith Christina Theodora |
发明人 |
van Deutekom Judith Christina Theodora |
分类号 |
C07H21/02;C07K14/00 |
主分类号 |
C07H21/02 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
Dordrecht NL |