发明名称 Treatment of sanfilippo syndrome type b
摘要 <p>Disclosed is a stable formulation comprising a recombinant alpha-N-acetyl-glucosaminidase (Naglu) protein at a concentration at or greater than 5 mg/ml, and wherein the formulation comprises no greater than 50 mM of phosphate.</p>
申请公布号 NZ605871(A) 申请公布日期 2015.02.27
申请号 NZ20110605871 申请日期 2011.06.25
申请人 SHIRE HUMAN GENETIC THERAPIES INC 发明人 CONCINO MICHAEL F.;HOLMES KEVIN;MARTINI PAOLO;ROMASHKO ALLA;MEIYAPPAN MUTHURAMAN;ZHANG BOHONG;ISKENDERIAN ANDREA;LUNDBERG DIANNA;NORTON ANGELA;STRACK-LOGUE BETTINA;HUANG YAN;ALESSANDRINI MARY;CALIAS PERICLES;PAN JING;PFEIFER RICHARD
分类号 A61K38/47;A61P25/00;A61P25/28 主分类号 A61K38/47
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