发明名称 |
Treatment of sanfilippo syndrome type b |
摘要 |
<p>Disclosed is a stable formulation comprising a recombinant alpha-N-acetyl-glucosaminidase (Naglu) protein at a concentration at or greater than 5 mg/ml, and wherein the formulation comprises no greater than 50 mM of phosphate.</p> |
申请公布号 |
NZ605871(A) |
申请公布日期 |
2015.02.27 |
申请号 |
NZ20110605871 |
申请日期 |
2011.06.25 |
申请人 |
SHIRE HUMAN GENETIC THERAPIES INC |
发明人 |
CONCINO MICHAEL F.;HOLMES KEVIN;MARTINI PAOLO;ROMASHKO ALLA;MEIYAPPAN MUTHURAMAN;ZHANG BOHONG;ISKENDERIAN ANDREA;LUNDBERG DIANNA;NORTON ANGELA;STRACK-LOGUE BETTINA;HUANG YAN;ALESSANDRINI MARY;CALIAS PERICLES;PAN JING;PFEIFER RICHARD |
分类号 |
A61K38/47;A61P25/00;A61P25/28 |
主分类号 |
A61K38/47 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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