| 发明名称 |
COMPOSITIONS AND METHODS FOR MODULATING EXPRESSION OF FRATAXIN |
| 摘要 |
Provided herein are compositions and methods for increasing Frataxin (FXN) expression. Compositions and methods for treating Friedrich's ataxia are also provided. |
| 申请公布号 |
WO2015023939(A1) |
申请公布日期 |
2015.02.19 |
| 申请号 |
WO2014US51261 |
申请日期 |
2014.08.15 |
| 申请人 |
RANA THERAPEUTICS, INC. |
发明人 |
OZSOLAK, FATIH |
| 分类号 |
C12N15/63;A61K38/17;A61P21/00;C07K14/47 |
主分类号 |
C12N15/63 |
| 代理机构 |
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