发明名称 |
RNA MODULATING OLIGONUCLEOTIDES WITH IMPROVED CHARACTERISTICS FOR THE TREATMENT OF DUCHENNE AND BECKER MUSCULAR DYSTROPHY |
摘要 |
The current invention provides an improved oligonucleotide and its use for treating, ameliorating, preventing and/or delaying DMD or BMD. |
申请公布号 |
EP2806900(A1) |
申请公布日期 |
2014.12.03 |
申请号 |
EP20130704832 |
申请日期 |
2013.01.28 |
申请人 |
PROSENSA TECHNOLOGIES B.V. |
发明人 |
DE VISSER, PETER CHRISTIAN;VAN DEUTEKOM, JUDITH CHRISTINA THEODORA |
分类号 |
A61K48/00;A61P21/00 |
主分类号 |
A61K48/00 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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