发明名称 |
ADENO-ASSOCIATED VIRUS MEDIATED GENE TRANSFER TO THE CENTRAL NERVOUS SYSTEM |
摘要 |
A method to prevent, inhibit or treat one or more symptoms associated with a disease of the central nervous system by intrathecally, intracerebroventricularly or endovascularly administering a rAAV encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease. |
申请公布号 |
WO2014186579(A1) |
申请公布日期 |
2014.11.20 |
申请号 |
WO2014US38209 |
申请日期 |
2014.05.15 |
申请人 |
REGENTS OF THE UNIVERSITY OF MINNESOTA |
发明人 |
MCIVOR, SCOTT R.;BELUR, LALITHA R.;LOW, WALTER;FAIRBANKS, CAROLYN |
分类号 |
A01N63/00;C12N15/00;C12N15/86 |
主分类号 |
A01N63/00 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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