| 发明名称 |
COMPOSITIONS AND METHODS FOR TREATING OCULOPHARYNGEAL MUSCULAR DYSTROPHY |
| 摘要 |
The present invention provides intravenous compositions of trehalose for the treatment of signs and symptoms of oculopharyngeal muscular dystrophy (OPMD). |
| 申请公布号 |
US2014336145(A1) |
申请公布日期 |
2014.11.13 |
| 申请号 |
US201414320184 |
申请日期 |
2014.06.30 |
| 申请人 |
BIOBLAST PHARMA LTD. |
发明人 |
MEGIDDO Dalia |
| 分类号 |
A61K9/00;A61K31/7016 |
主分类号 |
A61K9/00 |
| 代理机构 |
|
代理人 |
|
| 主权项 |
1. An aqueous formulation for intravenous injection comprising a single active ingredient consisting of trehalose, wherein the formulation has a pH about 4.5 to 7.0 and contains less than 0.75 endotoxin units per mL. |
| 地址 |
Tel Aviv IL |
