Methods and materials for treatment of Pompe's disease
摘要
This document relates to molecular complexes having acid alpha glucosidase activity and at least one modification that results in enhanced ability of the molecular complex to be transported to the interior of a mammalian cell.
申请公布号
AU2013234042(A1)
申请公布日期
2014.10.23
申请号
AU20130234042
申请日期
2013.03.14
申请人
OXYRANE UK LIMITED
发明人
VERVECKEN, WOUTER;PIENS, KATHLEEN CAMILLA TELESPHORE ALIDA MARIA;STOUT, JAN ROBERT LUDO;PYNAERT, GWENDA NOELLA