发明名称 ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS OF USE THEREOF
摘要 An antisense molecule capable of binding to a selected target site to induce exon skipping in the dystrophin gene, as set forth in SEQ ID NO: 1 to 202.
申请公布号 US2014309284(A1) 申请公布日期 2014.10.16
申请号 US201414316609 申请日期 2014.06.26
申请人 The University of Western Australia 发明人 Wilton Stephen Donald;Fletcher Sue;McClorey Graham
分类号 C12N15/113 主分类号 C12N15/113
代理机构 代理人
主权项
地址 Crawley AU