发明名称 |
ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS OF USE THEREOF |
摘要 |
An antisense molecule capable of binding to a selected target site to induce exon skipping in the dystrophin gene, as set forth in SEQ ID NO: 1 to 202. |
申请公布号 |
US2014309284(A1) |
申请公布日期 |
2014.10.16 |
申请号 |
US201414316609 |
申请日期 |
2014.06.26 |
申请人 |
The University of Western Australia |
发明人 |
Wilton Stephen Donald;Fletcher Sue;McClorey Graham |
分类号 |
C12N15/113 |
主分类号 |
C12N15/113 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
Crawley AU |