发明名称 |
COMPOUNDS FOR TREATING SPINAL MUSCULAR ATROPHY |
摘要 |
Provided herein are compounds, compositions thereof and uses therewith for treating spinal muscular atrophy. |
申请公布号 |
KR20140121482(A) |
申请公布日期 |
2014.10.15 |
申请号 |
KR20147025275 |
申请日期 |
2013.02.08 |
申请人 |
PTC THERAPEUTICS, INC.;F. HOFFMANN-LA ROCHE AG |
发明人 |
QI HONGYAN;CHOI SOONGYU;DAKKA AMAL;KARP GARY MITCHELL;NARASIMHAN JANA;NARYSHKIN NIKOLAI;TURPOFF ANTHONY A.;WEETALL MARLA L.;WELCH ELLEN;WOLL MATTHEW G.;YANG TIANLE;ZHANG NANJING;ZHANG XIAOYAN;ZHAO XIN;GREEN LUKE;PINARD EMMANUEL;RATNI HASANE |
分类号 |
C07D403/04;A61K31/519;C07D239/70;C07D471/04;C07D487/04 |
主分类号 |
C07D403/04 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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