| 发明名称 |
TREATMENT OPTIONS FOR FABRY DISEASE |
| 摘要 |
A formulation for use in the treatment of Fabry disease, wherein the formulation comprises a carrier and 1-deoxygalactonojirimycin or a salt thereof, characterized in that the 1-deoxygalactonojirimycin or a salt thereof is administered to a Fabry disease patient in an amount of 150 mg every other day. |
| 申请公布号 |
EP2787345(A1) |
申请公布日期 |
2014.10.08 |
| 申请号 |
EP20140168748 |
申请日期 |
2007.05.16 |
| 申请人 |
AMICUS THERAPEUTICS, INC.;NATIONAL INSTITUTES OF HEALTH |
发明人 |
LOCKHART, DAVID;CASTELLI, JEFF |
| 分类号 |
G01N33/53;A61K31/435;G01N33/567;G01N33/573 |
主分类号 |
G01N33/53 |
| 代理机构 |
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代理人 |
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