发明名称 MIR-204 AND MIR-211 AND USES THEREOF
摘要 The present invention relates to at least one agent capable of increasing the level of one or more miRNA in a cell or cells of a subject, said miRNA comprising the sequence UUCCCUU, for use in the treatment and/or prevention of a retinal dystrophy, in particular characterized by photoreceptor degeneration, relative pharmaceutical compositions, nucleic acids, vectors and host cells.
申请公布号 CA2904164(A1) 申请公布日期 2014.09.18
申请号 CA20142904164 申请日期 2014.03.11
申请人 FONDAZIONE TELETHON 发明人 SURACE, ENRICO MARIA;BANFI, SANDRO;CONTE, IVAN;KARALI, MARIANTHI;MARROCCO, ELENA
分类号 C12N15/113;A61K31/713;A61P27/02 主分类号 C12N15/113
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