发明名称 |
METHODS AND COMPOSITIONS FOR THE PREVENTION OR TREATMENT OF BARTH SYNDROME |
摘要 |
The disclosure provides methods of preventing or treating Barth Syndrome in a mammalian subject, reducing risk factors associated with Barth Syndrome, and/or reducing the likelihood or severity of Barth Syndrome. The methods comprise administering to the subject an effective amount of an aromatic-cationic peptide to increase expression of TAZ1 in subjects in need thereof. |
申请公布号 |
CA2916880(A1) |
申请公布日期 |
2014.09.04 |
申请号 |
CA20142916880 |
申请日期 |
2014.02.28 |
申请人 |
STEALTH BIOTHERAPEUTICS CORP |
发明人 |
WILSON, D. TRAVIS;BAMBERGER, MARK |
分类号 |
A61K38/06 |
主分类号 |
A61K38/06 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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