发明名称 |
ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS OF USE THEREOF |
摘要 |
An antisense molecule capable of binding to a selected target site to induce exon skipping in the dystrophin gene, as set forth in SEQ ID NO: 1 to 202. |
申请公布号 |
US2014243515(A1) |
申请公布日期 |
2014.08.28 |
申请号 |
US201414273318 |
申请日期 |
2014.05.08 |
申请人 |
THE UNIVERSITY OF WESTERN AUSTRALIA |
发明人 |
WILTON Stephen Donald;FLETCHER Sue;MCCLOREY Graham |
分类号 |
C12N15/113 |
主分类号 |
C12N15/113 |
代理机构 |
|
代理人 |
|
主权项 |
1. (canceled) |
地址 |
Crawley AU |