发明名称 Multiple exon skipping compositions for DMD
摘要 The present invention relates to an oligonucleotide which specifically hybridizes to a target region in an exon of the human dystrophin gene inducing exon skipping. The present invention further relates to a pharmaceutical composition comprising an oligonucleotide which specifically hybridizes to a target region in an exon of the human dystrophin gene inducing exon skipping.
申请公布号 EP2762567(A1) 申请公布日期 2014.08.06
申请号 EP20140157806 申请日期 2009.10.23
申请人 SAREPTA THERAPEUTICS, INC. 发明人 SAZANI, PETER;KOLE, RYSZARD
分类号 C12N15/113 主分类号 C12N15/113
代理机构 代理人
主权项
地址