发明名称 COMPOSITIONS AND METHODS FOR TREATING FRIEDREICH'S ATAXIA WITH INTERFERON GAMMA
摘要 Described herein are compositions and methods for treating Friedreich's Ataxia (FRDA) with interferon gamma. In some aspects, methods for increasing expression of frataxin in cells and for treating Friedreich's Ataxia are provided. In some additional aspects, methods increasing aconitase activity in cells are provided.
申请公布号 PT2611457(E) 申请公布日期 2014.06.05
申请号 PT20110805174T 申请日期 2011.08.30
申请人 ROBERTO TESTI;BARBARA TOMASSINI 发明人 ROBERTO TESTI;BARBARA TOMASSINI
分类号 A61K38/21;A61P25/00 主分类号 A61K38/21
代理机构 代理人
主权项
地址