发明名称 OLIGONUCLEOTIDE MODULATION OF SPLICING
摘要 The present invention relates to the selective modulation of pre-mRNA splicing, in particular, for that involving alternative splicing in disease-related proteins such as those involved in Duschenne's Muscular Dystropy and Spinal Muscular Atrophy.
申请公布号 US2014128449(A1) 申请公布日期 2014.05.08
申请号 US201214009745 申请日期 2012.03.23
申请人 LIU JING;HU JIAXIN;COREY DAVID R.;THE BOARD OF REGENTS OF THE UNIVERSITY OF TEXAS SYSTEM 发明人 LIU JING;HU JIAXIN;COREY DAVID R.
分类号 C12N15/113 主分类号 C12N15/113
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