发明名称 |
OLIGONUCLEOTIDE MODULATION OF SPLICING |
摘要 |
The present invention relates to the selective modulation of pre-mRNA splicing, in particular, for that involving alternative splicing in disease-related proteins such as those involved in Duschenne's Muscular Dystropy and Spinal Muscular Atrophy. |
申请公布号 |
US2014128449(A1) |
申请公布日期 |
2014.05.08 |
申请号 |
US201214009745 |
申请日期 |
2012.03.23 |
申请人 |
LIU JING;HU JIAXIN;COREY DAVID R.;THE BOARD OF REGENTS OF THE UNIVERSITY OF TEXAS SYSTEM |
发明人 |
LIU JING;HU JIAXIN;COREY DAVID R. |
分类号 |
C12N15/113 |
主分类号 |
C12N15/113 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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