发明名称 COMPOSITIONS AND METHODS FOR INHIBITING HEPCIDIN ANTIMICROBIAL PEPTIDE (HAMP) OR HAMP-RELATED GENE EXPRESSION
摘要 The invention relates to lipid formulated double-stranded ribonucleic acid (dsRNA) targeting a hepcidin antimicrobial peptide (HAMP) and/or HAMP-related gene, and methods of using the dsRNA to inhibit expression of HAMP and/or HAMP-related genes.
申请公布号 EP2723861(A2) 申请公布日期 2014.04.30
申请号 EP20120801896 申请日期 2012.06.21
申请人 ALNYLAM PHARMACEUTICALS, INC. 发明人 BETTENCOURT, BRIAN;AKINC, AKIN;SEHGAL, ALFICA;FOSTER, DON;MILSTEIN, STUART;KUCHIMANCHI, SATYA;MAIER, MARTIN;CHARISSE, KLAUS;RAJEEY, KALLANTHOTTATHIL
分类号 C12N15/113;A61K31/713 主分类号 C12N15/113
代理机构 代理人
主权项
地址