发明名称 TREATMENT OF WOLFRAM SYNDROME-RELATED NEURODEGENERATION
摘要 Provided is a method of treating and/or preventing Wolfram Syndrome (WS)-related neurodegeneration (i.e. of Wolfram Syndrome-Associated Neuronal Degeneration), by increasing the expression and/or functional activity of p21. A method of screening for pharmacological agents useful in treating and/or preventing such conditions is also provided.
申请公布号 WO2014049366(A1) 申请公布日期 2014.04.03
申请号 WO2013GB52523 申请日期 2013.09.27
申请人 THE UNIVERSITY OF BIRMINGHAM 发明人 NAGY, ZSUZSANNA;BARRETT, TIMOTHY
分类号 A61K31/436;A61K31/145;A61K31/19;A61K31/192;A61K31/4412;A61K31/4439;A61K31/451;A61K31/4706;A61K31/496;A61K31/575;A61P25/28 主分类号 A61K31/436
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