| 发明名称 |
MULTIPLE EXON SKIPPING COMPOSITIONS FOR DMD |
| 摘要 |
Provided are antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon skipping, and methods of use thereof to treat muscular dystrophy. |
| 申请公布号 |
US2014094500(A1) |
申请公布日期 |
2014.04.03 |
| 申请号 |
US201313829545 |
申请日期 |
2013.03.14 |
| 申请人 |
SAREPTA THERAPEUTICS, INC. |
发明人 |
SAZANI PETER;KOLE RYSZARD |
| 分类号 |
C12N15/113 |
主分类号 |
C12N15/113 |
| 代理机构 |
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代理人 |
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| 主权项 |
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| 地址 |
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