发明名称 EFFICIENT PROTEIN EXPRESSION IN VIVO USING MODIFIED RNA (MOD-RNA)
摘要 Aspects of the invention described herein relate to synthetic, modified RNAs and their use in vivo to modulate gene expression. Aspects of the invention further relate to the use of these synthetic, modified RNAs in myocytes, cardiomyoctes, and tumors.
申请公布号 US2014073687(A1) 申请公布日期 2014.03.13
申请号 US201214009351 申请日期 2012.03.12
申请人 CHIEN KENNETH R.;PTASZEK LEON M.;LUI KATHY OI-LAN;ZANGI LIOR;EBINA WATARU;ROSSI DERRICK J.;IMMUNE DISEASE INSTITUTE, INC.;THE GENERAL HOSPITAL CORPORATION 发明人 CHIEN KENNETH R.;PTASZEK LEON M.;LUI KATHY OI-LAN;ZANGI LIOR;EBINA WATARU;ROSSI DERRICK J.
分类号 A61K38/18 主分类号 A61K38/18
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