发明名称 |
AAV MEDIATED AQUAPORIN GENE TRANSER TO TREAT SJOGREN'S SYNDROME |
摘要 |
The invention relates to a gene transfer-based method to protect a subject from Sjogren's syndrome. The method comprises administering to the subject an AAV virion comprising an AAV vector that encodes aquaporin- 1 (AQP-1) protein. Also provided are AQP-1 proteins and nucleic acid molecules that encode such proteins. Also provided are AAV vectors and AAV virions that encode an AQP- 1 protein. |
申请公布号 |
WO2014036468(A2) |
申请公布日期 |
2014.03.06 |
申请号 |
WO2013US57632 |
申请日期 |
2013.08.30 |
申请人 |
THE UNITED STATES OF AMERICA, AS REPRESENTED BY THE SECRETARY, DEPARTMENT OF HEALTH & HUMAN SERVICES |
发明人 |
CHIORINI, JOHN |
分类号 |
C12N15/86;A61K48/00;C07K14/705 |
主分类号 |
C12N15/86 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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