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发明名称
摘要
The present invention provides isolated promoters, transgene expression cassettes, vectors, kits, and methods for treatment of genetic diseases that affect the cone cells of the retina.
申请公布号
JP2014504871(A)
申请公布日期
2014.02.27
申请号
JP20130548562
申请日期
2012.01.06
申请人
发明人
分类号
C12N15/09;A61K31/7088;A61K35/76;A61K48/00;A61P27/02;A61P43/00
主分类号
C12N15/09
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