发明名称 |
AAV8 Vector with Enhanced Functional Activity and Methods of Use Thereof |
摘要 |
Improved compositions and methods for AAV mediated gene therapy are disclosed. |
申请公布号 |
US2014037585(A1) |
申请公布日期 |
2014.02.06 |
申请号 |
US201213985351 |
申请日期 |
2012.02.14 |
申请人 |
WRIGHT JOHN FRASER;ZELENAIA OLGA;HAUCK BERND;MINGOZZI FEDERICO;HIGH KATHERINE A.;THE CHILDREN'S HOSPITAL OF PHILADELPHIA |
发明人 |
WRIGHT JOHN FRASER;ZELENAIA OLGA;HAUCK BERND;MINGOZZI FEDERICO;HIGH KATHERINE A. |
分类号 |
C12N15/86;A61K38/48;A61K48/00 |
主分类号 |
C12N15/86 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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