| 发明名称 |
OLIGONUCLEOTIDE ANALOGUES TARGETING HUMAN LMNA |
| 摘要 |
Provided are LMNA-targeted antisense oligonucleotides for reducing expression of one or more aberrantly spliced LMNA mRNA isoforms that encode progerin. |
| 申请公布号 |
US2014024821(A1) |
申请公布日期 |
2014.01.23 |
| 申请号 |
US201213708708 |
申请日期 |
2012.12.07 |
| 申请人 |
SAREPTA THERAPEUTICS, INC. |
发明人 |
KOLE RYSZARD;BESTWICK RICHARD KEITH |
| 分类号 |
C12N15/113 |
主分类号 |
C12N15/113 |
| 代理机构 |
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代理人 |
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| 主权项 |
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| 地址 |
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