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发明名称
IMPROVED AAV8 VECTOR WITH ENHANCED FUNCTIONAL ACTIVITY AND METHODS OF USE THEREOF
摘要
<p>Improved compositions and methods for AAV mediated gene therapy are disclosed.</p>
申请公布号
EP2675484(A2)
申请公布日期
2013.12.25
申请号
EP20120746664
申请日期
2012.02.14
申请人
THE CHILDREN'S HOSPITAL OF PHILADELPHIA RESEARCH INSTITUTE, ABRAMSON RESEARCH CENTER
发明人
WRIGHT, JOHN, FRASER;ZELENAIA, OLGA;HAUCK, BERND;MINGOZZI, FEDERICO;HIGH, KATHERINE, A.
分类号
A61K48/00
主分类号
A61K48/00
代理机构
代理人
主权项
地址
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