发明名称 IMPROVED AAV8 VECTOR WITH ENHANCED FUNCTIONAL ACTIVITY AND METHODS OF USE THEREOF
摘要 <p>Improved compositions and methods for AAV mediated gene therapy are disclosed.</p>
申请公布号 EP2675484(A2) 申请公布日期 2013.12.25
申请号 EP20120746664 申请日期 2012.02.14
申请人 THE CHILDREN'S HOSPITAL OF PHILADELPHIA RESEARCH INSTITUTE, ABRAMSON RESEARCH CENTER 发明人 WRIGHT, JOHN, FRASER;ZELENAIA, OLGA;HAUCK, BERND;MINGOZZI, FEDERICO;HIGH, KATHERINE, A.
分类号 A61K48/00 主分类号 A61K48/00
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