发明名称 Organic compositions to treat Beta-ENaC-related diseases
摘要 The present disclosure relates to RNAi agents useful in methods of treating Beta-ENaC-related diseases such as cystic fibrosis, pseudohypoaldosteronism type 1 (PHA1), Liddle's syndrome, hypertension, alkalosis, hypokalemia, and obesity-associated hypertension, using a therapeutically effective amount of a RNAi agent to Beta-ENaC.
申请公布号 US8598335(B2) 申请公布日期 2013.12.03
申请号 US201213614836 申请日期 2012.09.13
申请人 DE FOUGEROLLES ANTONIN;DIENER JOHN;HICKMAN EMMA;HINKLE GREGORY;MILSTEIN STUART;PULICHINO ANNE-MARIE;SPRAGUE ANDREW GRIFFIN;NOVARTIS AG 发明人 DE FOUGEROLLES ANTONIN;DIENER JOHN;HICKMAN EMMA;HINKLE GREGORY;MILSTEIN STUART;PULICHINO ANNE-MARIE;SPRAGUE ANDREW GRIFFIN
分类号 C07H21/04;A61K48/00;C07H21/02 主分类号 C07H21/04
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