发明名称 |
ANTISENSE OLIGONUCLEOTIDES FOR INDUCING EXON SKIPPING AND METHODS OF USE THEREOF |
摘要 |
Antisense molecules capable of binding to a selected target site in the dystrophin gene to induce exon skipping are described.
|
申请公布号 |
US2013253180(A1) |
申请公布日期 |
2013.09.26 |
申请号 |
US201313902376 |
申请日期 |
2013.05.24 |
申请人 |
THE UNIVERSITY OF WESTERN AUSTRALIA |
发明人 |
WILTON STEPHEN DONALD;FLETCHER SUE;MCCLOREY GRAHAM |
分类号 |
C12N15/113 |
主分类号 |
C12N15/113 |
代理机构 |
|
代理人 |
|
主权项 |
|
地址 |
|