发明名称 COMPOUND USEFUL FOR THE TREATMENT OF NONSENSE-MUTATION-MEDIATED DISEASES AND PHARMACEUTICAL COMPOSITION COMPRISING SAID COMPOUND
摘要 The present invention relates to the compound of formula (I) for use in the treatment of a nonsense-mutation-mediated genetic disease.
申请公布号 US2013217717(A1) 申请公布日期 2013.08.22
申请号 US201113813914 申请日期 2011.07.29
申请人 LEJEUNE FABRICE;DEPREZ BENOIT;BEGHYN TERENCE;GONZALEZ-HILARION SARA SOFIA;UNIVERSITE DE DROIT ET SANTE DE LILLE;INSTITUT PASTEUR DE LILLE;INSTITUT NATIONAL DE LA SANTE ET DE LA RECHERCHE MEDICALE (INSERM) 发明人 LEJEUNE FABRICE;DEPREZ BENOIT;BEGHYN TERENCE;GONZALEZ-HILARION SARA SOFIA
分类号 A61K31/436;A61K31/4245 主分类号 A61K31/436
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