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发明名称
COMPOUNDS FOR TREATING SPINAL MUSCULAR ATROPHY
摘要
Provided herein are compounds, compositions thereof and uses therewith for treating spinal muscular atrophy.
申请公布号
WO2013112788(A1)
申请公布日期
2013.08.01
申请号
WO2013US23067
申请日期
2013.01.25
申请人
PTC THERAPEUTICS, INC.
发明人
CHEN, GUANGMING;DAKKA, AMAL;KARP, GARY MITCHELL;LI, CHUNSHI;NARASIMHAN, JANA;NARYSHKIN, NIKOLAI;WEETALL, MARIA L.;WELCH, ELLEN;ZHAO, XIN
分类号
A61K31/44;A01N43/42
主分类号
A61K31/44
代理机构
代理人
主权项
地址
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