发明名称 ANTISENSE NUCLEIC ACID
摘要 <p>The present invention provides a pharmaceutical composition which causes skipping of the 53rd exon in the human dystrophin gene with a high efficiency. The present invention provides an oligomer which efficiently enables to cause skipping of the 53rd exon in the human dystrophin gene.</p>
申请公布号 EP2612917(A1) 申请公布日期 2013.07.10
申请号 EP20110821996 申请日期 2011.08.31
申请人 NIPPON SHINYAKU CO., LTD.;NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY 发明人 WATANABE, NAOKI;SATOU, YOUHEI;TAKEDA, SHIN'ICHI;NAGATA, TETSUYA
分类号 C12N15/113;A61K31/7125;C12N15/11 主分类号 C12N15/113
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