发明名称 |
ANTISENSE NUCLEIC ACID |
摘要 |
The purpose of the invention is to provide a drug to produce highly efficient skipping of exons 55, 45, 50, and 44 of a human dystrophin gene. The invention provides an oligomer that makes it possible to skip exons 55, 45, 50, and 44 of a human dystrophin gene. |
申请公布号 |
WO2013100190(A1) |
申请公布日期 |
2013.07.04 |
申请号 |
WO2012JP84295 |
申请日期 |
2012.12.27 |
申请人 |
NIPPON SHINYAKU CO., LTD.;NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY |
发明人 |
WATANABE, NAOKI;SEO, HARUNA;TAKEDA, SHIN'ICHI;NAGATA, TETSUYA |
分类号 |
C12N15/113;A61K31/7088;A61K48/00;A61P21/04;A61P43/00 |
主分类号 |
C12N15/113 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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