发明名称 ANTISENSE NUCLEIC ACID
摘要 The purpose of the invention is to provide a drug to produce highly efficient skipping of exons 55, 45, 50, and 44 of a human dystrophin gene. The invention provides an oligomer that makes it possible to skip exons 55, 45, 50, and 44 of a human dystrophin gene.
申请公布号 WO2013100190(A1) 申请公布日期 2013.07.04
申请号 WO2012JP84295 申请日期 2012.12.27
申请人 NIPPON SHINYAKU CO., LTD.;NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY 发明人 WATANABE, NAOKI;SEO, HARUNA;TAKEDA, SHIN'ICHI;NAGATA, TETSUYA
分类号 C12N15/113;A61K31/7088;A61K48/00;A61P21/04;A61P43/00 主分类号 C12N15/113
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