发明名称 SMALL MOLECULE CONJUGATES FOR INTRACELLULAR DELIVERY OF BIOLOGICALLY ACTIVE COMPOUNDS.
摘要 The invention provides novel compounds and conjugates of these compounds useful for the delivery of biologically active substances. Further novel design criteria for chemically stabilized siRNA particular useful when covalently attached to a delivery polymer to achieve in vivo mRNA knock down are disclosed therein.
申请公布号 MX2013006329(A) 申请公布日期 2013.06.28
申请号 MX20130006329 申请日期 2011.12.22
申请人 F. HOFFMANN-LA ROCHE AG 发明人 DAVID L. LEWIS;ERIC A. KITAS;DAVID B. ROZEMA;PETER MOHR;KERSTIN JAHN-HOFMANN;PHILIPP HADWIGER;TORSTEN HOFFMANN;HANS MARTIN MUELLER;GUENTHER OTT;INGO ROEHL
分类号 C12N15/87;A61K31/713;A61K47/18;A61K48/00;C12N15/11 主分类号 C12N15/87
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