发明名称 |
SMALL MOLECULE CONJUGATES FOR INTRACELLULAR DELIVERY OF BIOLOGICALLY ACTIVE COMPOUNDS. |
摘要 |
The invention provides novel compounds and conjugates of these compounds useful for the delivery of biologically active substances. Further novel design criteria for chemically stabilized siRNA particular useful when covalently attached to a delivery polymer to achieve in vivo mRNA knock down are disclosed therein. |
申请公布号 |
MX2013006329(A) |
申请公布日期 |
2013.06.28 |
申请号 |
MX20130006329 |
申请日期 |
2011.12.22 |
申请人 |
F. HOFFMANN-LA ROCHE AG |
发明人 |
DAVID L. LEWIS;ERIC A. KITAS;DAVID B. ROZEMA;PETER MOHR;KERSTIN JAHN-HOFMANN;PHILIPP HADWIGER;TORSTEN HOFFMANN;HANS MARTIN MUELLER;GUENTHER OTT;INGO ROEHL |
分类号 |
C12N15/87;A61K31/713;A61K47/18;A61K48/00;C12N15/11 |
主分类号 |
C12N15/87 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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