| 发明名称 |
ANTISENSE NUCLEIC ACID |
| 摘要 |
<p>The present invention provides a pharmaceutical composition which causes skipping of the 53rd exon in the human dystrophin gene with a high efficiency. The present invention provides an oligomer which efficiently enables to cause skipping of the 53rd exon in the human dystrophin gene.</p> |
| 申请公布号 |
KR20130069762(A) |
申请公布日期 |
2013.06.26 |
| 申请号 |
KR20137006385 |
申请日期 |
2011.08.31 |
| 申请人 |
NIPPON SHINYAKU CO., LTD.;NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY |
发明人 |
WATANABE NAOKI;SATOU YOUHEI;TAKEDA SHIN'ICHI;NAGATA TETSUYA |
| 分类号 |
C12N15/113;A61K31/7125;A61P21/04;C07H21/04 |
主分类号 |
C12N15/113 |
| 代理机构 |
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代理人 |
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| 主权项 |
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| 地址 |
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