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发明名称
OLIGONUCLEOTIDE ANALOGUES TARGETING HUMAN LMNA
摘要
Provided are LMNA-targeted antisense oligonucleotides for reducing expression of one or more aberrantly spliced LMNA mRNA isoforms that encode progerin.
申请公布号
WO2013086441(A2)
申请公布日期
2013.06.13
申请号
WO2012US68606
申请日期
2012.12.07
申请人
SAREPTA THERAPEUTICS, INC.
发明人
RYSZARD, KOLE;BESTWICK, RICHARD, KEITH
分类号
C12N15/113
主分类号
C12N15/113
代理机构
代理人
主权项
地址
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