COMPOUNDS AND METHODS FOR TREATING CYSTIC FIBROSIS

摘要

The invention features novel compounds useful for the treatment or prevention of cystic fibrosis. Further, the invention also relates to methods, kits and packaged compositions for the treatment or prevention of cystic fibrosis in a subject identified in need of a treatment of cystic fibrosis thereof. In particular embodiments, the compounds of the invention are capable of increasing CFTR expression level in a clinically significant amount in a cell membrane.