发明名称 COMPOSITIONS AND METHODS FOR INHIBITING HEPCIDIN ANTIMICROBIAL PEPTIDE (HAMP) OR HAMP-RELATED GENE EXPRESSION
摘要 The invention relates to lipid formulated double-stranded ribonucleic acid (dsRNA) targeting a hepcidm antimicrobial peptide (HAMP) and/or HAMP-related gene, and methods of using the dsRNA to inhibit expression of HAMP and/or HAMP-related genes.
申请公布号 WO2012177921(A2) 申请公布日期 2012.12.27
申请号 WO2012US43603 申请日期 2012.06.21
申请人 ALNYLAM PHARMACEUTICALS, INC;BETTENCOURT, BRIAN;AKINC, AKIN;SEHGAL, ALFICA;FOSTER, DON;MILSTEIN, STUART;KUCHIMANCHI, SATYA;MAIER, MARTIN;CHARISSE, KLAUS;KALLANTHOTTATHIL, RAJEEV 发明人 BETTENCOURT, BRIAN;AKINC, AKIN;SEHGAL, ALFICA;FOSTER, DON;MILSTEIN, STUART;KUCHIMANCHI, SATYA;MAIER, MARTIN;CHARISSE, KLAUS;KALLANTHOTTATHIL, RAJEEV
分类号 A61K48/00;A61K38/18 主分类号 A61K48/00
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