发明名称 COMPOSITIONS AND METHODS FOR TREATMENT OF SPINAL MUSCULAR ATROPHY
摘要 <p>Disclosed herein are compounds, compositions and methods for treatment of diseases and disorders, including spinal muscular atrophy.</p>
申请公布号 WO2012178146(A1) 申请公布日期 2012.12.27
申请号 WO2012US43946 申请日期 2012.06.25
申请人 ISIS PHARMACEUTICALS, INC.;COLD SPRING HARBOR LABORATORY;HUA, YIMIN;KRAINER, ADRIAN, R.;RIGO, FRANK;BENNETT, C., FRANK 发明人 HUA, YIMIN;KRAINER, ADRIAN, R.;RIGO, FRANK;BENNETT, C., FRANK
分类号 A61K38/30 主分类号 A61K38/30
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