摘要 |
Compounds, compositions and methods for the treatment of retinal degenerative diseases, such as retinitis pigmentosa, Leber's congenital Amaurosis, Syndromic retinal degenerations, age-related macular degeneration and Usher Syndrome, and hearing loss associated with Usher Syndrome are described herein. |
申请人 |
USHER III INITIATIVE;BURLI, ROLAND WERNER;ESMIEU, WILLIAM RAMESHCHANDRA KRISHNA;LOCK, CHRISTOPHER JAMES;MALAGU, KARINE FABIENNE;OWENS, ANDREW PATE;HARTE, WILLIAM EDWARD |
发明人 |
BURLI, ROLAND WERNER;ESMIEU, WILLIAM RAMESHCHANDRA KRISHNA;LOCK, CHRISTOPHER JAMES;MALAGU, KARINE FABIENNE;OWENS, ANDREW PATE;HARTE, WILLIAM EDWARD |