发明名称 |
Treatment of alpha-galactosidase A deficiency |
摘要 |
P:/OPER/HPMShN Humn,/3079158/Page 62.doc-3AO6/29 The invention provides methods of treating a-galactosidase A deficiency. Dosage forms, methods of administration, and methods of analyzing human a-galactosidase A are 5 also included. |
申请公布号 |
AU2009217430(B2) |
申请公布日期 |
2012.10.18 |
申请号 |
AU20090217430 |
申请日期 |
2009.09.22 |
申请人 |
SHIRE HUMAN GENETIC THERAPIES, INC. |
发明人 |
BOROWSKI, MARIANNE;TRECO, DOUGLAS A.;LOVEDAY, KENNETH |
分类号 |
C12N15/09;A61K35/16;A61K38/12;A61K38/46;A61K38/47;A61P9/00;A61P13/12;A61P25/04;A61P43/00;C12Q1/34;C12Q1/54 |
主分类号 |
C12N15/09 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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