Compounds for the treatment of spinal muscular atrophy and other uses
摘要
Compounds of Formula (I) or (Il) useful for the treatment of spinal muscular atrophy or other uses, as well as methods of using such compounds to increase SMN expression, increase EAAT2 expression, or increase the expression of a nucleic acid that encodes a translational stop codon introduced by mutation or frameshift.
申请公布号
AU2007227398(B2)
申请公布日期
2012.09.27
申请号
AU20070227398
申请日期
2007.03.16
申请人
ALBANY MOLECULAR RESEARCH, INC.;THE UNITED STATES OF AMERICA, AS REPRESENTED BY THE SECRETARY
发明人
JOHNSON, GRAHAM;HEEMSKERK, JILL;JOHNSON, MATTHEW ROBERT;MCCALL, JOHN M.;BARNES, KEITH D.;FAIRFAX, DAVID