The present invention is directed to RNA interference (RNAi) molecules targeted against a Huntington's disease nucleic acid sequence, and methods of using these RNAi molecules to treat Huntington's disease.
申请公布号
WO2012109667(A1)
申请公布日期
2012.08.16
申请号
WO2012US24904
申请日期
2012.02.13
申请人
UNIVERSITY OF IOWA RESEARCH FOUNDATION;DAVIDSON, BEVERLY, L.;BOUDREAU, RYAN, L.